Abbreviations
SAA severe aplastic anemia
IST immunosuppressive therapy
CR complete response
G-CSF granulocyte colony stimulating factor
EFS event-free survival
AA aplastic anemia
rATG rabbit anti-thymocyte globulin
CSA Cyclosporine
OR overall response
OS overall survival
FDA Food and Drug Administration
FISH fluorescence in situ hybridization
PNH paroxysmal nocturnal hemoglobinuria
PR partial response
NR no response
VSAA very severe aplastic anemia
HSCT hematopoietic stem cell transplantation
NIH National Institutes of Health