Acknowledgements
G.N.G declares grants from Instituto de Salud Carlos III (Grant Numbers: PI15/01756; P18/00713), Madrid, Spain and AFM Telethon (Trampoline grant number #21108), France. A.L declares grants from the Spanish government granting agency Instituto de Salud Carlos III, Madrid, Spain. J.N.M is funded by AFM Telethon Trampoline Grant #21108. A.B.L is funded by an FI Agaur fellowship FI_B 01090 and by SGR 1520. E.K is funded by the “La Caixa” Foundation (ID 100010434), fellowship code LCF/BQ/IN18/11660019, co-funded by the European Union ̵́s Horizon 2020 research and innovation program under the Marie Skłodowska-Curie grant agreement nº713673. I.L.P is funded by CP14/00032 and by SGR 1520. G.N.G is supported by a Miguel Servet research contract (ISCIII CD14/00032, CPII19/00021 and FEDER). G.L. was supported by a Rio Hortega contract (ISCIII CM16/00016 and FEDER). J.J-M was supported by the Science, Technology and Innovation of Mexico City (Grant # PICSA 12-162). This work was supported in part by a grant from the 2017 SGR288 and SGR 1520 (GRC) Generalitat de Catalunya; economic support from CERCA Programme/Generalitat de Catalunya and Fundació Internacional Josep Carreras.
G.P-M reports personal honoraria from Shire-Takeda, Amicus, Kyowa-Kirin, and Sanofi-Genzyme, outside the submitted work. The remaining co-authors declare no competing interests.
We gratefully acknowledge the participants in this research, the patient’s associations and the core facilities of the IGTP and Single Cell Unit from IJC. We acknowledge our funding agencies and Ruben Artero’s team for their advice on studying DMPK expression.