|
CLINICAL DATA
|
CLINICAL DATA
|
CLINICAL DATA
|
CLINICAL DATA
|
CLINICAL DATA
|
CLINICAL DATA
|
CLINICAL DATA
|
EXPANSION SIZE
|
EXPANSION SIZE
|
FOCI ANALYSIS
|
FOCI ANALYSIS
|
FOCI ANALYSIS
|
FOCI ANALYSIS
|
FOCI ANALYSIS
|
Patient
|
Age of onset
|
Age at sampling
|
Gender
|
mRS
|
MIRS
|
Biceps MRC
|
6MWT
|
Muscle
|
Myoblasts
|
No. of cells studied
|
% cells with foci
|
Mean
|
Median
|
Range
|
P1
|
15*
|
36
|
F
|
2
|
4
|
4
|
348
|
691
|
823
|
72
|
97,2%
|
2,3
|
2
|
0-6
|
P2
|
48
|
54
|
M
|
2
|
3
|
5
|
251
|
ND
|
ND
|
72
|
98,6%
|
2,6
|
2
|
0-7
|
P3
|
36
|
41
|
F
|
1
|
2
|
5
|
368
|
208
|
1686
|
63
|
81%
|
1,4
|
1
|
0-4
|
P4
|
27
|
39
|
F
|
4
|
4
|
4
|
NP
|
469
|
561
|
39
|
97,4%
|
2,7
|
3
|
0-5
|
P5
|
36
|
41
|
M
|
2
|
3
|
5
|
519
|
135
|
150
|
66
|
28,8%
|
0,6
|
0
|
0-7
|